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亮丙瑞林治疗肯尼迪病的开放式研究 被引量:6

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摘要 肯尼迪病的病因为位于Xq11-12的雄激素受体(androgen receptors,AR)基因发生突变。动物实验结果表明,亮丙瑞林可有效改善肯尼迪病转基因鼠的临床症状。为检验亮丙瑞林对于肯尼迪病患者的疗效,我们进行了亮丙瑞林治疗肯尼迪病的开放式临床研究。
出处 《中华神经科杂志》 CAS CSCD 北大核心 2013年第8期544-545,共2页 Chinese Journal of Neurology
基金 基金项目:国家自然科学基金青年基金资助项目(30700239)
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参考文献7

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二级参考文献19

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共引文献56

同被引文献80

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