血友病B基因治疗进展

Current opinion in gene therapy of haemophilia B

血友病B是一种严重的凝血功能缺陷遗传病 ,由于现行的治疗方法对血友病B的治疗效果均不令人满意。因此 ,有必要开展血友病的基因治疗研究。本文介绍了血友病B的发病机理以及以反转录病毒载体为工具进行血友病B基因治疗的研究进展。

Haemophilia b is a kind of serious cruor-defective inhering diseaes.So it is necessary to develop its cure method for the current method is not ideal.This review focused on Haemophilia B's mechanism and the new development of retrovirus vector used in the gene therapy of Haemophilis B.