基于定价和补偿角度探讨罕用药价格规制体系

Discussion about the orphan drug pricing regulation system from the perspective of pricing and reimbursement

本文主要通过对罕见病用药的属性及其市场竞争特点进行分析,从公共产品角度明确罕见病用药需要保障其可及性和减轻罕见病患者的用药负担,进而从补偿机制和定价机制分析了我国罕见病用药的价格规制体系,明确其存在的问题,通过对台湾和日本的罕见药品规制体系进行分析,最后提出如何完善我国罕见病药品的价格规制体系。

This paper analyzed the property and market competition features of orphan drugs, clarified the need to ensure the accessibility of orphan drugs and reduce the burden on patients based on the fact that orphan drugs are public goods. We then analyzed the pricing regulation system of orphan drug from the perspective of reim- bursement and pricing mechanism, and pointed out its problems. Finally we analyzed the rare drugs regulation sys- tems in Taiwan and Japan, and proposed how to improve our orphan drug pricing regulation system.