罕见病药物研究现状分析与展望

Analysis and prospect of status of orphan drug research

社会对罕见病关注的日益增加推动了政府关于罕见病立法的工作进展,一系列罕见病相关政策陆续出台。然而受经济、人口、社会保障水平等条件制约,中国罕见病的医疗保障和药物研究仍处于起步阶段。本文阐述并分析了罕见病药物研究的现状及未来的发展情况,为罕见病政策制订和产业发展提供参考。

Growing attention on the rare diseases promotes the work of the government legislation,so a series of rare diseases related policies have been introduced. However,under the conditions of economy,population,social security and so on,China′s rare disease medical care and drug development are still in the initial stage. This paper elaborates and analyzes the status and future development of rare disease drugs,and provides advice for the policy formation of rare diseases and industrial development.