摘要
在一项促使基因疗法新时代早日降临的决定当中,美国食品药品监督管理局(FDA)核准了一种修正脱氧核糖核酸(DNA)的药物,这种药物能够逆转一种遗传性的渐进式失明。
In a decision that accelerates a new era for gene therapy, the Food and Drug Administration [(FDA)] approved a DNA-altering medication that can reverse an inherited form of progressive blindness.