iPSC-based treatment of age-related macular degeneration (AMD):The path to success requires more than blind faith
摘要
Induced pluripotent stem cells(iPSCs)hold great promise for the treatment of human diseases.Two recent first-of-its-kind clinical case reports on the iPSC-based treatment of age-related macular degeneration(AMD)highlight the hopes and challenges associated with the clinical application of iPSCs.
基金
Work in the authors’laboratories was supported in part by research grants from the National Institutes of Health(AT004418 to TCH)
from the Canadian Institutes of Health Research(MOP 125882 to JH)
a Cystic Fibrosis Foundation Therapeutics,Inc.grant(HU15XX0 to JH)
a Cystic Fibrosis Canada grant(#3032 to JH).
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